Company Sector
Rare Disease Gene Therapy
Rare Disease Gene Therapy is a company sector tag on BioPharmSignal. This page groups public biotech and healthcare companies associated with Rare Disease Gene Therapy, making it easier to scan related businesses, compare peers, and follow companies exposed to the same modality, disease area, or development theme.
Why watch Rare Disease Gene Therapy
This page combines a company index, a watch action, and the newest relevant feed items in one place so readers can monitor a biotech theme without scanning each company one by one.
Latest Rare Disease Gene Therapy news
The latest feed items from companies currently grouped under Rare Disease Gene Therapy.
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ABEOAbeona Therapeutics® to Host Second Quarter 2026 Financial Results Conference Call on August 13, 2026
Source: Abeona Therapeutics
- 03
EDITEditas Medicine Announces Second Quarter 2026 Results and Business Updates
Source: Editas Medicine
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ABEOCMS Grants New Technology Add-On Payment (NTAP) Status for ZEVASKYN®
Source: Abeona Therapeutics
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ABEOAbeona Therapeutics® Announces New Employee Inducement Grants Under Nasdaq Listing Rule 5635(c)(4)
Source: Abeona Therapeutics
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KRYSKrystal Biotech Announces Second Quarter 2026 Financial and Operating Results
Source: Krystal Biotech
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KRYSKrystal Biotech to Report Second Quarter 2026 Financial Results on August 3, 2026
Source: Krystal Biotech
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ABEOCincinnati Children's Activated as the Seventh Qualified Treatment Center for ZEVASKYN®
Source: Abeona Therapeutics
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ABEOAbeona Therapeutics® Announces New Employee Inducement Grants Under Nasdaq Listing Rule 5635(c)(4)
Source: Abeona Therapeutics
- 13
RCKTRocket Pharmaceuticals Announces Closing of Sale of Rare Pediatric Disease Priority Review Voucher for $180 Million
Source: Rocket Pharmaceuticals
- 14
ABEOAbeona Therapeutics® Announces New Employee Inducement Grants Under Nasdaq Listing Rule 5635(c)(4)
Source: Abeona Therapeutics
- 15
EDITEditas Medicine Announces Updated Presentation Time for Upcoming Investor Conference
Source: Editas Medicine
- 16
RCKTRocket Pharmaceuticals to Participate in Upcoming Investor Conferences
Source: Rocket Pharmaceuticals
- 17
EDITEditas Medicine Announces Pricing of Up to $319.4 Million Public Offering
Source: Editas Medicine
- 18
ABEOAbeona Therapeutics® Announces Participation in Upcoming Investor Conferences
Source: Abeona Therapeutics
- 19
EDITEditas Medicine Announces Proposed Public Offering
Source: Editas Medicine
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Companies in Rare Disease Gene Therapy
10 companies tagged with Rare Disease Gene Therapy.
Frequently Asked Questions
What does the Rare Disease Gene Therapy sector include?
Rare Disease Gene Therapy is a company sector tag on BioPharmSignal. This page groups public biotech and healthcare companies associated with Rare Disease Gene Therapy, making it easier to scan related businesses, compare peers, and follow companies exposed to the same modality, disease area, or development theme.
How many companies are currently tagged with Rare Disease Gene Therapy?
10 companies are currently grouped under Rare Disease Gene Therapy on BioPharmSignal.
Which companies are most visible in the Rare Disease Gene Therapy group right now?
ABEO, AVRO, BMRN, CCBS are among the companies currently shown on this sector page.
How can I watch news for Rare Disease Gene Therapy?
Use the Watch button on this page to subscribe to Rare Disease Gene Therapy headlines and related company updates through your BioPharmSignal saved filters.
What kinds of updates usually appear for Rare Disease Gene Therapy?
The livefeed typically surfaces company press releases, clinical readouts, FDA and regulatory updates, partnerships, financings, and commercialization developments tied to companies in Rare Disease Gene Therapy.